Page 99 - 南京医科大学自然版
P. 99
第44卷第7期 周 寅,俞 静,丁国宪. 肠道类器官基因编辑技术的研究进展[J].
2024年7月 南京医科大学学报(自然科学版),2024,44(7):979-984 ·983 ·
[12]LIN L,DEMARTINO J,WANG D,et al. Unbiased tran⁃ [25]HORII T,MORITA S,KIMURA M,et al. Efficient genera⁃
scription factor CRISPR screen identifies ZNF800 as master tion of epigenetic disease model mice by epigenome edit⁃
repressor of enteroendocrine differentiation[J]. Science, ing using the piggyBac transposon system[J]. Epigenetics
2023,382(6669):451-458 Chromatin,2022,15(1):40
[13]WANG J Y,DOUDNA J A. CRISPR technology:a decade [26]GU J,ROLLO B,BERECKI G,et al. Generation of a stably
of genome editing is only the beginning[J]. Science, transfected mouse embryonic stem cell line for inducible
2023,379(6629):eadd8643 differentiation to excitatory neurons[J]. Exp Cell Res,
[14]CHEHELGERDI M,CHEHELGERDI M,KHORRAMIAN⁃ 2024,435(1):113902
GHAHFAROKHI M,et al. Comprehensive review of [27]岳 冉,刘子洋,郑 岩,等. 纳米载体介导的PiggyBac
CRISPR ⁃ based gene editing:mechanisms,challenges, 转座子制备 CAR⁃NK 细胞[J]. 中国肿瘤生物治疗杂
and applications in cancer therapy[J]. Mol Cancer,2024, 志,2020,27(2):109-114
23(1):9 [28]姜淇耀,史甲儒,罗志强,等. 基于PiggyBac转座系统的
[15]TAKEDA H,KATAOKA S,NAKAYAMA M,et al. CRIS⁃ CD19⁃CAR 载体的构建及功能鉴定[J]. 中国肿瘤生物
PR ⁃ Cas9 ⁃ mediated gene knockout in intestinal tumor 治疗杂志,2023,30(2):156-160
organoids provides functional validation for colorectal [29]EGGENSCHWILER R,GSCHWENDTBERGER T,FELS⁃
cancer driver genes[J]. Proc Natl Acad Sci U S A,2019, KI C,et al. A selectable all⁃in⁃one CRISPR prime editing
116(31):15635-15644 piggyBac transposon allows for highly efficient gene edit⁃
[16]GU W,COLARUSSO J L,DAME M K,et al. Rapid estab⁃ ing in human cell lines[J]. Sci Rep,2021,11(1):22154
lishment of human colonic organoid knockout lines[J]. [30]SUN Y,LIU G,HUANG Y. Applications of piggyBac
STAR Protoc,2022,3(2):101308 transposons for genome manipulation in stem cells[J].
[17] RUTHERFORD D,HO G T. Therapeutic potential of Stem Cells Int,2021,2021:3829286
human intestinal organoids in tissue repair approaches in [31]MANGEOT P E,RISSON V,FUSIL F,et al. Genome edit⁃
inflammatory bowel diseases[J]. Inflamm Bowel Dis, ing in primary cells and in vivo using viral⁃derived Nano⁃
2023,29(9):1488-1498 blades loaded with Cas9 ⁃ sgRNA ribonucleoproteins[J].
[18]SCHWANK G,ANDERSSON⁃ROLF A,KOO B K,et al. Nat Commun,2019,10(1):45
Generation of BAC transgenic epithelial organoids[J]. [32]GUTIERREZ⁃GUERRERO A,ABREY RECALDE M J,
PLoS One,2013,8(10):e76871 MANGEOT P E,et al. Baboon envelope pseudotyped
[19]SHIZUYA H,BIRREN B,KIM U J,et al. Cloning and stable “nanoblades”carryingCas9/gRNAcomplexesallowefficient
+
maintenance of 300 ⁃ kilobase ⁃ pair fragments of human genome editing in human T,B,and CD34 cells and knock⁃in
+
DNA in Escherichia coli using an F⁃factor⁃based vector[J]. of AAV6⁃encoded donor DNA in CD34 cells[J]. Front
Proc Natl Acad Sci U S A,1992,89(18):8794-8797 Genome Ed,2021,3:604371
[20]ZIMMER W E,SCHWARTZ R J. Transient transgenics: [33]BERNADIN O,AMIRACHE F,GIRARD⁃GAGNEPAIN
an efficient method to identify gene regulatory elements[J]. A,et al. Baboon envelope LVs efficiently transduced
Methods Mol Biol,2021,2319:119-136 human adult,fetal,and progenitor T cells and corrected
[21]HEINTZ N,GONG S. Working with bacterial artificial SCID⁃X1 T⁃cell deficiency[J]. Blood Adv,2019,3(3):
chromosomes(BACs)and other high⁃capacity vectors[J]. 461-475
Cold Spring Harb Protoc,2020,2020(10):doi:10.1101/ [34]TIROILLE V,KRUG A,BOKOBZA E,et al. Nanoblades
pdb.top097998 allow high ⁃ level genome editing in murine and human
[22] TERIYAPIROM I,BATISTA ⁃ ROCHA A S,KOO B K. organoids[J]. Mol Ther Nucleic Acids,2023,33:57-74
Genetic engineering in organoids[J]. J Mol Med(Berl), [35]GEBOERS B,SCHEFFER H J,GRAYBILL P M,et al.
2021,99(4):555-556 High ⁃ voltage electrical pulses in oncology:irreversible
[23]TSAI HC,PIETROBON V,PENG M,et al. Current strate⁃ electroporation,electrochemotherapy,gene electrotransfer,
gies employed in the manipulation of gene expression for electrofusion,and electroimmunotherapy. radiology[J].
clinical purposes[J]. J Transl Med,2022,20(1):535 Radiology,2020,295(2):254-272
[24]LIN SC,HAGA K,ZENG XL,et al. Generation of CRIS⁃ [36]CAMPELO S N,HUANG P H,BUIE C R,et al. Recent
PR ⁃ Cas9 ⁃ mediated genetic knockout human intestinal advancements in electroporation technologies:from bench
tissue ⁃ derived enteroid lines by lentivirus transduction to clinic[J]. Annu Rev Biomed Eng,2023,25:77-100
and single⁃cell cloning[J]. Nat Protoc,2022,17(4):1004- [37]DE CARO A,BELLARD E,KOLOSNJAJ⁃TABI J,et al.
1027 Gene electrotransfer efficiency in 2D and 3D cancer cell